Posts by Arne Lauer, MD
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Hematopoietic Stem-Cell Gene Therapy Restores White Matter Microvascular Function in Cerebral Adrenoleukodystrophy
Arne Lauer, MD, Patricia L. Musolino, MD, PhD, and colleagues found that ABCD1 gene therapy with autologous hematopoietic stem cells halts the progression of cerebral adrenoleukodystrophy at least in part because it improves microvascular circulation of the entire cerebral white matter.
Biography
Arne Lauer, MD, is a researcher in the department of neurology at Massachusetts General Hospital.